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OncoMatch/Clinical Trials/NCT05948943

Alpelisib in Pediatric and Adult Patients With Lymphatic Malformations Associated With a PIK3CA Mutation.

Is NCT05948943 recruiting? Yes, currently enrolling (May 2026). This Phase 2/3 trial studies Alpelisib for lymphatic malformations.

Phase 2/3RecruitingNovartis PharmaceuticalsNCT05948943Data as of May 2026

Treatment: AlpelisibThe main purpose of this study in participants with PIK3CA-mutated LyM is to assess the change in radiological response and symptom severity upon treatment with alpelisib film-coated tablets (FCT) as compared to placebo.

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Extracted eligibility criteria

Biomarker criteria

Required: PIK3CA somatic mutation

evidence of a somatic mutation(s) in the PIK3CA gene prior to randomization

Prior therapy

Cannot have received: PI3K inhibitor (alpelisib)

Exception: treatment duration longer than 2 weeks

previous treatment with alpelisib and/or any other PI3K inhibitors with treatment duration longer than 2 weeks

Structured fields extracted by AI. May contain errors — verify against the official protocol.

US trial sites

  • UCSF Benioff Children s Hospital · Oakland, California
  • Lucile Packard Childrens Hosp · Palo Alto, California
  • Childrens National Medical Center · Washington D.C., District of Columbia
  • Childrens Hosp Boston Dept of Heme · Boston, Massachusetts
  • WA Uni School Of Med · St Louis, Missouri

Showing up to 5 US sites. See all sites on ClinicalTrials.gov →

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