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OncoMatch/Clinical Trials/NCT05658640

HEM iSMART-D: Trametinib + Dexamethasone + Chemotherapy in Children With Relapsed or Refractory Hematological Malignancies

Is NCT05658640 recruiting? Yes, currently enrolling (Jun 2026). This Phase 1/2 trial studies multiple treatments for acute lymphoblastic leukemia, in relapse.

Phase 1/2RecruitingPrincess Maxima Center for Pediatric OncologyNCT05658640Data as of Jun 2026Location: International · 15 countries

Treatment: Trametinib · Dexamethasone · Cyclophosphamide · Cytarabine · Intrathecal chemotherapyHEM-iSMART is a master protocol which investigates multiple investigational medicinal products in children, adolescents and young adults (AYA) with relapsed/refractory (R/R) ALL and LBL. Sub-protocol D is a phase I/II trial evaluating the safety and efficacy of trametinib in combination with dexamethasone, cyclophosphamide and cytarabine in children and AYA with R/R ped ALL/LBL whose tumor present with alterations in the RAS-RAF-MAPK pathway.

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Extracted eligibility criteria

Treatments studied

Targeted therapy

Trametinib

Chemotherapy

CyclophosphamideCytarabine

Other

DexamethasoneIntrathecal chemotherapy

Cancer type

Acute Lymphoblastic Leukemia

Non-Hodgkin Lymphoma

Biomarker criteria

Required: KRAS activating mutation

RAS pathway activating mutations including but not limited to KRAS, NRAS, HRAS, FLT3, PTPN11, MAP2K1, MP2K1 hotspot mutations, cCBL; NF1 del

Required: NRAS activating mutation

RAS pathway activating mutations including but not limited to KRAS, NRAS, HRAS, FLT3, PTPN11, MAP2K1, MP2K1 hotspot mutations, cCBL; NF1 del

Required: HRAS activating mutation

RAS pathway activating mutations including but not limited to KRAS, NRAS, HRAS, FLT3, PTPN11, MAP2K1, MP2K1 hotspot mutations, cCBL; NF1 del

Required: FLT3 activating mutation

RAS pathway activating mutations including but not limited to KRAS, NRAS, HRAS, FLT3, PTPN11, MAP2K1, MP2K1 hotspot mutations, cCBL; NF1 del

Required: PTPN11 activating mutation

RAS pathway activating mutations including but not limited to KRAS, NRAS, HRAS, FLT3, PTPN11, MAP2K1, MP2K1 hotspot mutations, cCBL; NF1 del

Required: MAP2K1 hotspot mutation

RAS pathway activating mutations including but not limited to KRAS, NRAS, HRAS, FLT3, PTPN11, MAP2K1, MP2K1 hotspot mutations, cCBL; NF1 del

Required: MP2K1 hotspot mutation

RAS pathway activating mutations including but not limited to KRAS, NRAS, HRAS, FLT3, PTPN11, MAP2K1, MP2K1 hotspot mutations, cCBL; NF1 del

Required: CBL activating mutation

RAS pathway activating mutations including but not limited to KRAS, NRAS, HRAS, FLT3, PTPN11, MAP2K1, MP2K1 hotspot mutations, cCBL; NF1 del

Required: NF1 deletion

RAS pathway activating mutations including but not limited to KRAS, NRAS, HRAS, FLT3, PTPN11, MAP2K1, MP2K1 hotspot mutations, cCBL; NF1 del

Demographics

Ages 1–21

Prior therapy

Cannot have received: MEK inhibitor (trametinib)

Previous treatment with trametinib

Lab requirements

Kidney function

Serum creatinine ≤ 1.5 x ULN for age or calculated creatinine clearance as per the Schwartz formula or radioisotope GFR ≥ 60 mL/min/1.73 m2

Liver function

Direct bilirubin ≤ 2 x ULN (≤ 3.0 × ULN for patients with Gilbert's syndrome); ALT/SGPT ≤ 5 x ULN; AST/SGOT ≤ 5 x ULN. Patients with hepatic dysfunction related to underlying disease may be eligible after sponsor discussion.

Cardiac function

Shortening fraction (SF) >29% (>35% for children < 3 years) and/or LVEF ≥50% at baseline by echocardiography or MUGA; absence of QTcF prolongation (>450 msec on baseline ECG, Fridericia correction), or other clinically significant ventricular or atrial arrhythmia

RENAL AND HEPATIC FUNCTION (Assessed within 48 hours prior to C1D1): Serum creatinine ≤ 1.5 x ULN for age or calculated creatinine clearance as per the Schwartz formula or radioisotope GFR ≥ 60 mL/min/1.73 m2. Direct bilirubin ≤ 2 x ULN (≤ 3.0 × ULN for patients with Gilbert's syndrome). ALT/SGPT ≤ 5 x ULN; AST/SGOT ≤ 5 x ULN. Patients with hepatic dysfunction related to underlying disease may be eligible after sponsor discussion. CARDIAC FUNCTION: SF >29% (>35% for children < 3 years) and/or LVEF ≥50% at baseline by echocardiography or MUGA; absence of QTcF prolongation (>450 msec on baseline ECG, Fridericia correction), or other clinically significant ventricular or atrial arrhythmia.

Structured fields extracted by AI. May contain errors — verify against the official protocol.

Frequently asked questions

Is NCT05658640 currently recruiting?

Yes, this trial is currently recruiting patients.

Are there prior therapy exclusions?

Yes. Prior MEK inhibitor disqualifies patients from enrollment.

Does this trial require KRAS?

Yes, KRAS activating mutation is a required biomarker for enrollment.

Does this trial require NRAS?

Yes, NRAS activating mutation is a required biomarker for enrollment.

Does this trial require HRAS?

Yes, HRAS activating mutation is a required biomarker for enrollment.

Is there an age limit?

Yes. Patients must be 21 years or younger and at least 1 years old.

Could you qualify for this trial?

Enter your biomarker results to see how this trial's eligibility criteria match your specific cancer profile.

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