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OncoMatch/Clinical Trials/NCT05465174

Tovorafenib for Treatment of Craniopharyngioma in Children and Young Adults

Is NCT05465174 recruiting? Yes, currently enrolling (May 2026). This Phase 2 trial studies Tovorafenib for craniopharyngioma, child.

Phase 2RecruitingSabine Mueller, MD, PhDNCT05465174Data as of May 2026

Treatment: TovorafenibThe current study assesses the tolerability and efficacy of monotherapy with pan-RAF-kinase (Tovorafenib) inhibition for the treatment of children and young adults with craniopharyngioma.

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Extracted eligibility criteria

Cancer type

Glioblastoma

Prior therapy

Cannot have received: tumor-directed therapy

Newly Diagnosed Participants: Participants should not have undergone any previous tumor-directed therapy.

Cannot have received: RAS-pathway inhibitor

Exception: have not received Tovorafenib will be eligible

Participants should not have previously received any RAS-pathway, but have not received Tovorafenib will be eligible.

Lab requirements

Blood counts

ANC >=1000/mm3; Platelet count >= 100,000/mm3 (transfusion independent, defined as not receiving platelet transfusions for at least 7 days prior to enrollment)

Kidney function

Serum creatinine < 1.5 ULN based on age and gender

Liver function

Bilirubin (sum of conjugated + unconjugated) <= 1.5 x ULN for age (except in participants with documented Gilbert syndrome); ALT <= 3 x ULN; Serum albumin >=2 g/dL (20g/L)

Cardiac function

No clinically significant active cardiovascular disease, or history of myocardial infarction, or deep vein thrombosis/pulmonary embolism within 6 months prior to registration, ongoing cardiomyopathy, or current prolonged QTcF interval > 440 ms based on triplicate ECG average

Adequate Bone Marrow Function...Adequate Renal Function...Adequate Liver Function...Adequate Neurologic Function...Adequate Pulmonary Function...PT/PTT/INR within institutional normal limits or deemed appropriate for surgical intervention by the treating team for patients undergoing surgery biopsy/resection

Structured fields extracted by AI. May contain errors — verify against the official protocol.

US trial sites

  • University of Alabama at Birmingham · Birmingham, Alabama
  • Rady Children's Hospital/University of California, San Diego · San Diego, California
  • University of California, San Francisco · San Francisco, California
  • University of Florida · Gainesville, Florida
  • Ann & Robert H. Lurie Children's Hospital of Chicago · Chicago, Illinois

Showing up to 5 US sites. See all sites on ClinicalTrials.gov →

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