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OncoMatch/Clinical Trials/NCT04901936

A Study of Pegcetacoplan in Pediatric Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

Is NCT04901936 recruiting? Yes, currently enrolling (Jun 2026). This Phase 2 trial studies Pegcetacoplan for paroxysmal nocturnal hemoglobinuria (pnh).

Phase 2RecruitingApellis Pharmaceuticals, Inc.NCT04901936Data as of Jun 2026Location: International · 9 countries

Treatment: PegcetacoplanThe purpose of this study is to evaluate the safety, effectiveness, and biological activity (how the investigational medication is processed by the body) of pegcetacoplan in 12-17 year-olds (adolescents) who have paroxysmal nocturnal hemoglobinuria (PNH).

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Extracted eligibility criteria

Treatments studied

Other

Pegcetacoplan

Demographics

Ages 12–17

Lab requirements

Blood counts

platelet count >75,000/mm3 and absolute neutrophil count >1000/mm3

Have a platelet count >75,000/mm3 and an absolute neutrophil count >1000/mm3

Structured fields extracted by AI. May contain errors — verify against the official protocol.

US trial sites

  • Children's Hospital of Atlanta · Atlanta, Georgia

Showing up to 5 US sites.

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Frequently asked questions

Is NCT04901936 currently recruiting?

Yes, this trial is currently recruiting patients.

Is there an age limit?

Yes. Patients must be 17 years or younger and at least 12 years old.

Could you qualify for this trial?

Enter your biomarker results to see how this trial's eligibility criteria match your specific cancer profile.

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