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OncoMatch/Clinical Trials/NCT04681417

Ocular Conservative Treatment for Retinoblastoma : Efficacy of the New Management Strategies and Visual Outcome

Is NCT04681417 recruiting? Yes, currently enrolling (Jun 2026). This Phase 2/3 trial studies multiple treatments for retinoblastoma.

Phase 2/3RecruitingInstitut CurieNCT04681417Data as of Jun 2026Location: France

Treatment: Melphalan or Melphalan + Topotecan · etoposide, carboplatin and vincristine or local ophthalmological treatment without IV chemotherapy · Carboplatin administered on Day 1 · Thermotherapy (local treatment) · Cryotherapy (local treatment) · Iodine-125 plaques (local treatment) · Intravitreal Melphalan chemotherapy injections (local treatment)This protocol includes 2 independent studies. Both studies are multicenter studies, evaluating different therapeutic approaches in two different populations of patients: * Study 1, a randomized phase-II study evaluating the efficacy of Intra-Arterial Chemotherapy (IAC) with melphalan and topotecan versus melphalan alone, both in association with ophthalmologic treatments. * Study 2, a minimally invasive interventional study evaluating the results on visual function following reference treatment with intravenous (IV) chemotherapy in association with ophthalmologic or local ophthalmological treatment without IV chemotherapy.

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Extracted eligibility criteria

Treatments studied

Chemotherapy

etoposide, carboplatin and vincristine or local ophthalmological treatment without IV chemotherapyCarboplatin administered on Day 1

Other

Melphalan or Melphalan + TopotecanThermotherapy (local treatment)Cryotherapy (local treatment)Iodine-125 plaques (local treatment)Intravitreal Melphalan chemotherapy injections (local treatment)

Disease stage

Required: Stage GROUP A, GROUP B, GROUP C, GROUP D, GROUP E (International Intraocular Retinoblastoma Classification)

Excluded: Stage GROUP E WITH INVASION OF THE ANTERIOR SEGMENT, GROUP E WITH MASSIVE TUMOR OF MORE THAN 2/3 OF THE EYE

Unilateral Retinoblastoma classified as group B, C (if vitreous seeds < 3 mm), D or E with no invasion of the anterior segment, and without massive tumor of more than 2/3 of the eye, eligible for conservative management, or Bilateral Retinoblastoma but with very unbalanced lesions between the two eyes: one eye group D or E without invasion of the anterior segment or massive tumor of more than 2/3 of the eye, eligible for IAC, and the other eye eligible for local treatment only (without IAC).

Demographics

Ages 0–6

Prior therapy

No prior treatment (treatment-naive required)
Max 0 prior lines

Cannot have received: chemotherapy

Patients not previously treated with chemotherapy or radiotherapy for this or any other cancer.

Cannot have received: radiotherapy

Patients not previously treated with chemotherapy or radiotherapy for this or any other cancer.

Structured fields extracted by AI. May contain errors — verify against the official protocol.

Frequently asked questions

Is NCT04681417 currently recruiting?

Yes, this trial is currently recruiting patients.

Can patients have received prior systemic therapy?

No. This trial requires treatment-naive patients — prior systemic therapy is an exclusion criterion.

What disease stage is eligible?

Stage GROUP A or GROUP B or GROUP C or GROUP D or GROUP E is required.

Is there an age limit?

Yes. Patients must be 6 years or younger and at least 0 years old.

Could you qualify for this trial?

Enter your biomarker results to see how this trial's eligibility criteria match your specific cancer profile.

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