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OncoMatch/Clinical Trials/NCT04644211

Ruxolitinib in Thrombocythemia and Polycythemia Vera

Is NCT04644211 recruiting? Yes, currently enrolling (Jun 2026). This Phase 2 trial studies Ruxolitinib for essential thrombocythemia.

Phase 2RecruitingMassachusetts General HospitalNCT04644211Data as of Jun 2026

Treatment: RuxolitinibThis research is being done to see if the drug ruxolitinib is effective in reducing the symptoms caused by low-risk essential thrombocythemia (ET) and polycythemia vera (PV). \- This research study involves the study drug Ruxolitinib.

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Extracted eligibility criteria

Treatments studied

Targeted therapy

Ruxolitinib

Cancer type

Myeloproliferative Neoplasm

Biomarker criteria

Required: JAK2 V617F

presence of JAK2 mutation

Required: JAK2 wild-type

no JAK2 mutation

Performance status

ECOG 0–2(Ambulatory, capable of self-care)

Prior therapy

Cannot have received: investigational agent

Participants who are receiving any other investigational agents.

Lab requirements

Blood counts

leukocytes ≥3,000/mcL; absolute neutrophil count ≥1,500/mcL; platelets ≥100,000/mcL

Kidney function

creatinine ≤ institutional ULN OR glomerular filtration rate (GFR) ≥60 mL/min/1.73 m2 unless data exists supporting safe use at lower kidney function values, no lower than 30 mL/min/1.73 m2

Liver function

total bilirubin ≤ institutional upper limit of normal (ULN); AST(SGOT)/ALT(SGPT) ≤3 × institutional ULN

Cardiac function

NYHA Functional Classification class 2B or better

Participants must have adequate organ and marrow function as defined below: leukocytes ≥3,000/mcL; absolute neutrophil count ≥1,500/mcL; platelets ≥100,000/mcL; total bilirubin ≤ institutional upper limit of normal (ULN); AST(SGOT)/ALT(SGPT) ≤3 × institutional ULN; creatinine ≤ institutional ULN OR glomerular filtration rate (GFR) ≥60 mL/min/1.73 m2 unless data exists supporting safe use at lower kidney function values, no lower than 30 mL/min/1.73 m2. ... participants should be class 2B or better.

Structured fields extracted by AI. May contain errors — verify against the official protocol.

US trial sites

  • Massachusetts General Hospital · Boston, Massachusetts
  • Beth-Israel Deaconess Medical Center · Boston, Massachusetts
  • Dana Farber Cancer Institute · Boston, Massachusetts
  • Massachusetts General North Shore Cancer Center · Danvers, Massachusetts

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See all sites on ClinicalTrials.gov →

Frequently asked questions

Is NCT04644211 currently recruiting?

Yes, this trial is currently recruiting patients.

Are there prior therapy exclusions?

Yes. Prior investigational agent disqualifies patients from enrollment.

Does this trial require JAK2?

Yes, JAK2 V617F is a required biomarker for enrollment.

Does this trial require JAK2?

Yes, JAK2 wild-type is a required biomarker for enrollment.

Could you qualify for this trial?

Enter your biomarker results to see how this trial's eligibility criteria match your specific cancer profile.

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